| GENE_SYMBOL |
DRUG_NAME |
Ki (nM) |
IC50 (nM) |
Kd (nM) |
EC50 (nM) |
Potency (nM) |
AC50 (nM) |
Datasource |
| GBA |
(3S,4R,5R)-3,4,5-trihydroxy-1-(6-propoxyhexyl)piperidin-2-one |
NA |
127000 |
NA |
NA |
NA |
NA |
TTD |
| GBA |
(3S,4R,5R)-3,4,5-trihydroxy-1-(2-propoxyethyl)piperidin-2-one |
NA |
500000 |
NA |
NA |
NA |
NA |
TTD |
| GBA |
(3S,4R,5R)-1-[2-(dipropylamino)ethyl]-3,4,5-trihydroxypiperidin-2-one |
NA |
253000 |
NA |
NA |
NA |
NA |
TTD |
| GBA |
(3R,4R,5R)-1-decyl-3,4,5-trihydroxypiperidin-2-one |
NA |
463000 |
NA |
NA |
NA |
NA |
TTD |
| GBA |
N-[(3S,4R,5R)-1-decyl-4,5-dihydroxy-6-oxopiperidin-3-yl]acetamide |
NA |
500000 |
NA |
NA |
NA |
NA |
TTD |
| GBA |
(3R,4R)-1-decyl-3,4-dihydroxypyrrolidin-2-one |
NA |
285000 |
NA |
NA |
NA |
NA |
TTD |
| GBA |
(3R,4R,5R)-3,4,5-trihydroxy-1-(6-hydroxyhexyl)piperidin-2-one |
NA |
500000 |
NA |
NA |
NA |
NA |
TTD |
| GBA |
N-[(3S,4R,5R)-4,5-dihydroxy-1-(6-hydroxyhexyl)-6-oxopiperidin-3-yl]acetamide |
NA |
500000 |
NA |
NA |
NA |
NA |
TTD |
| GBA |
(3R,4R)-3,4-dihydroxy-1-(6-hydroxyhexyl)pyrrolidin-2-one |
NA |
500000 |
NA |
NA |
NA |
NA |
TTD |
| GBA |
(3R,5R)-1-octylpiperidine-3,4,5-triol |
NA |
500000 |
NA |
NA |
NA |
NA |
TTD |
| GBA |
(1R,2S,3r,4R,5S,6s)-6-[(1-Butyl-1H-1,2,3-triazol-4-yl)methylamino]cyclohexane-1,2,3,4,5-pentaol |
NA |
177827.94 |
NA |
NA |
NA |
NA |
TTD |
| GBA |
(1R,2S,3r,4R,5S,6s)-6-[2-(1-Octyl-1H-1,2,3-triazol-4-yl)ethylamino]cyclohexane-1,2,3,4,5-pentaol |
NA |
165958.69 |
NA |
NA |
NA |
NA |
TTD |
| GBA |
(1R,2S,3r,4R,5S,6s)-6-(3-(1-hexyl-1H-1,2,3-triazol-4-yl)propylamino)cyclohexane-1,2,3,4,5-pentaol |
NA |
257000 |
NA |
NA |
NA |
NA |
TTD |
| GBA |
(2S,3S,4R,5R,6S)-2-butyl-6-(hydroxymethyl)piperidine-3,4,5-triol |
NA |
147000 |
NA |
NA |
NA |
NA |
TTD |
| GBA |
Lucerastat |
NA |
320000 |
NA |
NA |
NA |
NA |
TTD |
| GBA |
Miglustat |
NA |
118000 |
NA |
NA |
NA |
NA |
TTD |
| GBA |
(1R,2S,4R,5S)-6-[[1-[(2-butyl-1H-imidazol-5-yl)methyl]triazol-4-yl]methylamino]cyclohexane-1,2,3,4,5-pentol |
NA |
237000 |
NA |
NA |
NA |
NA |
TTD |
| GBA |
rel-(1R,2S,4R,5S)-6-((1-((1-methyl-1H-benzo[d][1,2,3]triazol-6-yl)methyl)-1H-1,2,3-triazol-4-yl)methylamino)cyclohexane-1,2,3,4,5-pentaol |
NA |
114000 |
NA |
NA |
NA |
NA |
TTD |
| GBA |
rel-(1R,2S,4R,5S)-6-((1-(3-hydroxy-2,2-dimethylpropyl)-1H-1,2,3-triazol-4-yl)methylamino)cyclohexane-1,2,3,4,5-pentaol |
NA |
134000 |
NA |
NA |
NA |
NA |
TTD |
| GBA |
rel-(1R,2S,4R,5S)-6-((1-(3-(3-methoxypropoxy)propyl)-1H-1,2,3-triazol-4-yl)methylamino)cyclohexane-1,2,3,4,5-pentaol |
NA |
466000 |
NA |
NA |
NA |
NA |
TTD |